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Industry Profile

Gene Therapy

Target researchers — Molecular biologists and bioengineers in viral vectors, genome editing, delivery, and translational medicine

Gene therapy delivers genetic fixes for inherited and acquired diseases using viral vectors and genome editing. It recruits molecular biologists and bioengineers from academia and frequently licenses university-developed editing and delivery technologies.

$95B Market size
10 Key companies
5 Use cases

Key Companies

Spark Therapeutics Sarepta Therapeutics BioMarin uniQure Sangamo Therapeutics Intellia Therapeutics Beam Therapeutics Editas Medicine Krystal Biotech Solid Biosciences

Use Cases

01

AAV vector-engineering R&D hiring

02

CRISPR delivery partnerships

03

University gene-therapy-lab spin-outs

04

GMP and translational talent pipeline

05

Rare-disease research collaborations

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